| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 1 | |||
| NCT07290062 | A Study to Investigate the Safety and Pharmacodynamics of a Single Intrathecal Injection… | Amyotrophic Lateral Sclerosis | Recruiting |
| NCT06817382 | A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT)… | Duchenne Muscular Dystrophy | Recruiting |