| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 2 | |||
| NCT05935202 | Safety and Efficacy of Mitapivat Sulfate in Adult Patients With Erythrocyte… | Hereditary Red Blood Cell Disorder (Disorder) | Not Yet Recruiting |
| NCT07331818 | Luspatercept in Patients Affected With Rare Inherited Anemias | Hereditary Red Blood Cell Disorder (Disorder) | Not Yet Recruiting |