| Phase 1 | 1 | |
| Phase 1/2 | 1 | |
| Phase 2 | 1 |
| NCT ID | Title | Condition | Status | Updated |
|---|---|---|---|---|
| Phase 2 | ||||
| NCT05353647 | A Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN… | Sickle Cell Disease | Active, Not Recruiting | 2026-08-25 |
| Phase 1/2 | ||||
| NCT03311503 | Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan… | Severe Combined Immunodeficiency, X Linked | Recruiting | 2025-12-11 |
| Phase 1 | ||||
| NCT03282656 | Gene Transfer for Sickle Cell Disease | Sickle Cell Disease | Active, Not Recruiting | 2026-01-09 |
Sickle Cell Disease (2) · Thalassemia (2)