| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 2 | |||
| NCT05353647 | A Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN… | Sickle Cell Disease | Active, Not Recruiting |
| Phase 1/2 | |||
| NCT03311503 | Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan… | Severe Combined Immunodeficiency, X Linked | Recruiting |
| Phase 1 | |||
| NCT03282656 | Gene Transfer for Sickle Cell Disease | Sickle Cell Disease | Active, Not Recruiting |