| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 1 | |||
| NCT06647979 | Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies | Sickle Cell Disease | Recruiting |
| NCT07708350 | Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Sickle Cell Disease | Sickle Cell Disease | Not Yet Recruiting |