| Phase 1 | 1 | |
| Phase 3 | 2 |
| NCT ID | Title | Condition | Status | Updated |
|---|---|---|---|---|
| Phase 3 | ||||
| NCT05453968 | Berotralstat Treatment in Children With Hereditary Angioedema | Hereditary Angioedema | Active, Not Recruiting | 2026-02-25 |
| NCT04933721 | Open-label Berotralstat Access to HAE Patients Previously Enrolled in Berotralstat Studies | Hereditary Angioedema | Enrolling by Invitation | 2025-12-23 |
| Phase 1 | ||||
| NCT06539507 | A Study of the Safety, Tolerability, Pharmacokinetics, and Immunogenicity of BCX17725 | Netherton Syndrome | Recruiting | 2026-08-27 |