| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 2 | |||
| NCT03579875 | Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders | Fanconi Anemia | Recruiting |
| NCT03674411 | Trial Evaluating MGTA-456 in Patients With High-Risk Malignancy | Acute Myeloid Leukemia | Active, Not Recruiting |
| Phase 1/2 | |||
| NCT05463133 | Allogeneic Hematopoietic Stem Cell Transplantation for Chronic Granulomatous Disease… | Chronic Granulomatous Disease | Recruiting |