Trials about this condition or a more specific one, based on ClinicalTrials.gov's categories.
Top sponsors: Biogen (4) · Hugo W. Moser Research Institute at Kennedy Krieger, Inc. (4) · Centre Hospitalier Universitaire de Nice (3) · Lexeo Therapeutics (3) · University of California, San Francisco (3)
Data updated daily from ClinicalTrials.gov.