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Open-Label Study to Evaluate the Safety, Tolerability, and Efficacy of Gene Therapy (SPVN20) in Subjects With Rod-Cone Dystrophy

Study acronym: NYRVANA
StatusRecruiting
PhasePhase 1/2
Started
View on ClinicalTrials.gov ↗

Record History

  1. Minor Study First Submitted
This open-label, multi-center study is to evaluate the safety, tolerability, and efficacy of escalating doses of a gene therapy called SPVN20 administered via a single intravitreal injection in participants with advanced Rod-Cone Dystrophy.
Trial Details
NCT Number NCT07807111
Lead Sponsor SparingVision
Conditions
(from sponsor)
Retinitis Pigmentosa (RP), Rod Cone Dystrophy
Related terms Cone-Rod Dystrophies, Eye Diseases, Retinal Degeneration, Retinal Diseases, Retinal Dystrophies, Retinitis Pigmentosa
Enrollment 27 participants
Start Date
Primary Completion (estimated)
Study Completion (estimated)
Updated on ClinicalTrials.gov