Clinical Trial

Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA)

Name: Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA) — clinical trial record (NCT07681713)
Creator: DataLookout
License: https://creativecommons.org/licenses/by/4.0/

Study acronym: PROVE-FA

Not Yet Recruiting Phase 3

View on ClinicalTrials.gov →

Summary

The purpose of this study is to confirm the treatment effects of vatiquinone on the key measures of FA disease progression.

Protocol Amendment History 1 change

notable Trial sites expanded: 0 -> 9 locations 2026-08-15

Trial Details

NCT Number	NCT07681713
Lead Sponsor	PTC Therapeutics
Conditions	Friedreich's Ataxia
Enrollment	120 participants
Start Date	2026-08-15
Primary Completion	2029-03-15 (estimated)
Study Completion	2029-03-15 (estimated)
Updated on ClinicalTrials.gov	2026-08-14