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NCT07579910
Clinical Trial
Intracerebroventricular Tralesinidase Alfa in Participants With MPS IIIB (Sanfilippo Syndrome Type B)
Study acronym:
TrAnsform
Not Yet Recruiting
Phase 3
View on ClinicalTrials.gov →
Summary
The primary objectives of this study are to evaluate the effects of Tralesinidase Alfa (TA) on cognition
Trial Details
NCT Number
NCT07579910
Lead Sponsor
Spruce Biosciences
Conditions
MPS IIIB
Enrollment
14 participants
Start Date
2026-12
Primary Completion
2033-08
(estimated)
Study Completion
2033-08
(estimated)
Updated on ClinicalTrials.gov
2026-07-30