Clinical Trial

Intracerebroventricular Tralesinidase Alfa in Participants With MPS IIIB (Sanfilippo Syndrome Type B)

Study acronym: TrAnsform
Not Yet Recruiting Phase 3
View on ClinicalTrials.gov →
Summary
The primary objectives of this study are to evaluate the effects of Tralesinidase Alfa (TA) on cognition
Trial Details
NCT Number NCT07579910
Lead Sponsor Spruce Biosciences
Conditions MPS IIIB
Enrollment 14 participants
Start Date 2026-12
Primary Completion 2033-08 (estimated)
Study Completion 2033-08 (estimated)
Updated on ClinicalTrials.gov 2026-07-30