Clinical Trial

A Phase 2 Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Major

Not Yet Recruiting Phase 2
View on ClinicalTrials.gov →
Summary
The goal of this open label, single-arm clinical study is to learn about the safety and efficacy of CS-101 in treating patients with β-Thalassemia Major
Trial Details
NCT Number NCT07489196
Lead Sponsor CorrectSequence Therapeutics Co., Ltd
Conditions β-thalassemia Major
Enrollment 20 participants
Start Date 2026-04-05
Primary Completion 2028-01-31 (estimated)
Study Completion 2028-07-31 (estimated)
Updated on ClinicalTrials.gov 2026-03-24