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A Phase 2 Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Major

StatusNot Yet Recruiting
PhasePhase 2
Started
View on ClinicalTrials.gov ↗

Record History

  1. Minor Study First Submitted
The goal of this open label, single-arm clinical study is to learn about the safety and efficacy of CS-101 in treating patients with β-Thalassemia Major
Trial Details
NCT Number NCT07489196
Lead Sponsor CorrectSequence Therapeutics Co., Ltd
Conditions
(from sponsor)
β-thalassemia Major
Enrollment 20 participants
Start Date
Primary Completion (estimated)
Study Completion (estimated)
Updated on ClinicalTrials.gov