| NCT Number | NCT07488338 |
| Lead Sponsor | Teachers College, Columbia University |
| Conditions | Spinal Muscular Atrophy (SMA) |
| Enrollment | 20 participants |
| Start Date | 2026-03-15 |
| Primary Completion | 2028-02-28 (estimated) |
| Study Completion | 2028-12-31 (estimated) |
| Updated on ClinicalTrials.gov | 2026-03-23 |