Clinical Trial

Quality of Life in Pediatric Participants With HHT

Not Yet Recruiting
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Summary
This observational study evaluates health-related quality of life (HR-QoL) in pediatric and young adult patients aged 2-25 years with Hereditary Hemorrhagic Telangiectasia (HHT). Eligible participants are patients receiving care at Cincinnati Children's Hospital Medical Center and / or their caregivers. Participants will complete validated quality-of-life questionnaires assessing physical, emotional, social, and disease-specific functioning over the past 30 days. A paired retrospective chart review will assess disease severity and clinical utilization, including procedures and imaging studies. The primary objective is to describe mean QoL scores for this population. Secondary objectives include evaluating associations between QoL scores, disease severity, and clinical utilization.
Trial Details
NCT Number NCT07474428
Lead Sponsor Ashley Nelson
Conditions Hereditary Haemorrhagic Telangiectasia (HHT)
Enrollment 70 participants
Start Date 2026-07
Primary Completion 2026-12 (estimated)
Study Completion 2027-08 (estimated)
Updated on ClinicalTrials.gov 2026-03-16