Clinical Trial

A Real-World Study of Clinical Use of Available Treatments for Pediatric Patients With Spinal Muscular Atrophy

Completed
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Summary
The aim of this study was to evaluate real-world treatment patterns and clinical outcomes in pediatric SMA patients in the Czech and Slovak Republics, using data from the Registry of muscular Dystrophy (REaDY).
Protocol Amendment History 1 amendment
This ClinicalTrials.gov record has been amended once since 2026-03-11.
Trial Details
NCT Number NCT07474311
Lead Sponsor Novartis Pharmaceuticals
Conditions Muscular Atrophy, Spinal
Enrollment 213 participants
Start Date 2011-11-22
Primary Completion 2025-03-13 (estimated)
Study Completion 2025-03-13 (estimated)
Updated on ClinicalTrials.gov 2026-03-20