Clinical Trial

Prenatal Transplantation for Fetuses With Fanconi Anemia

Not Yet Recruiting Phase 1/2
View on ClinicalTrials.gov →
Summary
The investigators aim to evaluate the safety and efficacy of in utero hematopoietic stem cell transplantation (IUHSCT) for the treatment of fetuses diagnosed with Fanconi anemia (FA) during pregnancy.
Protocol Amendment History 2 changes
notable Primary completion pushed: 2030-07 -> 2031-07 2026-06-17
minor Completion pushed: 2032-07 -> 2033-07 2026-06-17
Trial Details
NCT Number NCT07408583
Lead Sponsor Agnieszka Czechowicz
Collaborators: University of California, San Francisco
Conditions Fanconi Anemia, Anemia, Hypoplastic, Congenital, Congenital Bone Marrow Failure Syndromes, Bone Marrow Failure Disorders, Genetic Diseases, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, Cancer Predisposition Syndrome
Enrollment 12 participants
Start Date 2028-01
Primary Completion 2031-07 (estimated)
Study Completion 2033-07 (estimated)
Updated on ClinicalTrials.gov 2026-06-16