Clinical Trial

Donidalorsen Treatment in Children With Hereditary Angioedema

Name: Donidalorsen Treatment in Children With Hereditary Angioedema — clinical trial record (NCT07298447)
Creator: DataLookout
License: https://creativecommons.org/licenses/by/4.0/

Recruiting Phase 3

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Summary

The purpose of this study is to evaluate the safety, tolerability and pharmacokinetics of donidalorsen in pediatric participants with hereditary angioedema (HAE) Type I (HAE-1) or Type II (HAE-2).

Protocol Amendment History 1 change

notable Trial sites expanded: 10 -> 13 locations 2026-08-06

Trial Details

NCT Number	NCT07298447
Lead Sponsor	Ionis Pharmaceuticals, Inc.
Conditions	Hereditary Angioedema (HAE)
Enrollment	20 participants
Start Date	2026-04-21
Primary Completion	2029-06 (estimated)
Study Completion	2029-06 (estimated)
Updated on ClinicalTrials.gov	2026-08-05