Clinical Trial

Ex Vivo Evaluation of JAK-inhibitor and Gene Therapeutical Approach in JAK-STAT Related Disorders

Study acronym: JAKarta
Recruiting
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Summary
The investigators want to study the JAK-inhibitors and their impact on the immune system and evaluate the potential of a gene-therapeutic strategy
Trial Details
NCT Number NCT07261891
Lead Sponsor prof. dr. Rik Schrijvers
Collaborators: Research Foundation - Flanders (Fonds Wetenschappelijk Onderzoek)
Conditions Primary Immunodeficiency Diseases (PID)
Enrollment 20 participants
Start Date 2024-11-21
Primary Completion 2028-12-01 (estimated)
Study Completion 2030-12-01 (estimated)
Updated on ClinicalTrials.gov 2025-12-03