CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain

The goal of this observational study is to set up a longitudinal data collection study to perform a long-term follow-up of SMA patients in a real-world setting, and to standardise and homogenize the data collection process for SMA patient's data. Treated and untreated patients will be followed based on the routine clinical practice schedule.

NCT Number	NCT07231549
Lead Sponsor	Fundació Sant Joan de Déu
Conditions	Spinal Muscular Atrophy
Enrollment	1,000 participants
Start Date	2020-05-05
Primary Completion	2026-12 (estimated)
Study Completion	2026-12 (estimated)
Updated on ClinicalTrials.gov	2025-11-17