Clinical Trial

Patients With Congenital Myasthenic Syndrome Will be Treated With Mesenchymal Stem Cell Exosome Solution

Recruiting Phase 1
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Summary
Patients with Congenital Myasthenic Syndrome will be treated with Mesenchymal Stem Cell Exosome solution.
Trial Details
NCT Number NCT07226726
Lead Sponsor The Foundation for Orthopaedics and Regenerative Medicine
Conditions Congenital Myasthenic Syndrome
Enrollment 20 participants
Start Date 2025-01-01
Primary Completion 2028-12-31 (estimated)
Study Completion 2028-12-31 (estimated)
Updated on ClinicalTrials.gov 2025-11-10