| NCT Number | NCT07226726 |
| Lead Sponsor | The Foundation for Orthopaedics and Regenerative Medicine |
| Conditions | Congenital Myasthenic Syndrome |
| Enrollment | 20 participants |
| Start Date | 2025-01-01 |
| Primary Completion | 2028-12-31 (estimated) |
| Study Completion | 2028-12-31 (estimated) |
| Updated on ClinicalTrials.gov | 2025-11-10 |