| NCT Number | NCT07223489 |
| Lead Sponsor | Medstar Health Research Institute |
| Conditions | Spinal Muscular Atrophy (SMA) |
| Enrollment | 200 participants |
| Start Date | 2025-10-10 |
| Primary Completion | 2026-06-30 (estimated) |
| Study Completion | 2026-12-30 (estimated) |
| Updated on ClinicalTrials.gov | 2026-01-16 |