| NCT Number | NCT07173010 |
| Lead Sponsor | Assiut University |
| Conditions | Mucopolysaccharidoses, Progressive Pseudorheumatoid Dysplasia, Farber Disease, Osteogenesis Imperfecta, Infantile Systemic Hyalinosis, Idiopathic Multicentric Osteolysis |
| Enrollment | 35 participants |
| Start Date | 2025-09 |
| Primary Completion | 2026-09 (estimated) |
| Study Completion | 2026-10 (estimated) |
| Updated on ClinicalTrials.gov | 2025-09-15 |