Clinical Trial

Prospective, Long Term, Observational Study (Patient Registry) of Paediatric Myotonic Disorders

Recruiting
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Summary
This is a prospective, open-label, multi-centre, single arm, registry study to collect standard relevant clinical and epidemiological data during routine medical evaluation and treatment in paediatric patients with myotonic disorders who are being treated with mexiletine therapy according to the physician.
Protocol Amendment History 1 amendment
This ClinicalTrials.gov record has been amended once since 2025-08-26.
Trial Details
NCT Number NCT07154654
Lead Sponsor Lupin Ltd.
Conditions Myotonic Disorders
Enrollment 10 participants
Start Date 2025-09-30
Primary Completion 2027-11-22 (estimated)
Study Completion 2028-02-22 (estimated)
Updated on ClinicalTrials.gov 2025-09-23