Clinical Trial

Validation of a Questionnaire for Quality of Life Assessment in Patients With Transthyretin Amyloidosis.

Active, Not Recruiting
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Record status
This record was last updated July 23, 2025 (before its estimated September 1, 2025 completion). Its status may not reflect the trial's current state.
Summary
Prospective study of development and validation of a questionnaire on quality of life in patients with Hereditary Amyloidosis The questionnaire development process will include 4 medical specialists experts in Transthyretin Amyloidosis (2 neurologists, 1 cardiologist, 1 physician clinical/hepathologist), 1 psychologist; 1 social worker; and 3 patients (with confirmed Hereditary amyloidosis) members of ALAPA. (Local PAG) Population and sample:
Trial Details
NCT Number NCT07080268
Lead Sponsor Hospital General de Niños Pedro de Elizalde
Conditions Amyloidosis in Transthyretin (TTR), Hereditary Amyloidosis, Transthyretin-Related
Enrollment 70 participants
Start Date 2025-06-20
Primary Completion 2025-09-01 (estimated)
Study Completion 2025-12-30 (estimated)
Updated on ClinicalTrials.gov 2025-07-23