Clinical Trial

Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia

Study acronym: CANOPY-HCH-EXT
Enrolling by Invitation Phase 3
View on ClinicalTrials.gov →
Summary
The purpose of this study is to evaluate the long-term safety and efficacy of daily doses of vosoritide in participants with HCH
Trial Details
NCT Number NCT07073014
Lead Sponsor BioMarin Pharmaceutical
Conditions Hypochondroplasia
Enrollment 140 participants
Start Date 2025-06-20
Primary Completion 2040-12 (estimated)
Study Completion 2040-12 (estimated)
Updated on ClinicalTrials.gov 2025-07-18