Clinical Trial

First-in-Human Clinical Trial of STUP-001, an In Vivo Direct Cell Conversion Gene Therapy for AIS-A/B Chronic Spinal Cord Injury

Study acronym: STUP-001
Recruiting Phase 1/2
View on ClinicalTrials.gov →
Summary
This study aim to investigate the safety and exploratory efficacy of STUP-001 which is AAV-based spinal cord injury investigational product.
Protocol Amendment History 2 amendments
This ClinicalTrials.gov record has been amended 2 times since 2025-04-03; most recent amendment 2025-07-10.
Status change: Not Yet Recruiting → Recruiting 2025-07-10
Trial Details
NCT Number NCT06922890
Lead Sponsor Yonsei University
Collaborators: Stand Up Therapeutics INC.
Conditions Spinal Cord Injury, Chronic Spinal Cord Injury
Enrollment 9 participants
Start Date 2025-07-30
Primary Completion 2026-12-31 (estimated)
Study Completion 2027-12-31 (estimated)
Updated on ClinicalTrials.gov 2025-07-16