Clinical Trial

Post-authorization Safety Study of Iptacopan in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Using Data From the IPIG PNH Registry

Active, Not Recruiting
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Summary
This is an observational single-arm descriptive cohort study based on the secondary use of data collected on iptacopan-treated patients with paroxysmal nocturnal hemoglobinuria (PNH) through the International PNH Interest Group (IPIG) PNH registry.
Protocol Amendment History 2 amendments
This ClinicalTrials.gov record has been amended 2 times since 2025-03-24; most recent amendment 2026-06-19.
Status change: Not Yet Recruiting → Active, Not Recruiting 2025-05-12
Trial Details
NCT Number NCT06903234
Lead Sponsor Novartis Pharmaceuticals
Conditions Hemoglobinuria, Paroxysmal
Enrollment 200 participants
Start Date 2025-03-31
Primary Completion 2029-10-01 (estimated)
Study Completion 2029-10-01 (estimated)
Updated on ClinicalTrials.gov 2026-06-23