Clinical Trial

Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients With Duchenne Muscular Dystrophy

Name: Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients With Duchenne Muscular Dystrophy — clinical trial record (NCT06900049)
Creator: DataLookout
License: https://creativecommons.org/licenses/by/4.0/

Recruiting Early Phase 1

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Summary

The purpose of this study is to evaluate the safety, tolerability, and efficacy of LE051 intravenous therapy in DMD patients treated with exon 51 skipping therapy.

Protocol Amendment History 1 amendment

This ClinicalTrials.gov record has been amended once since 2025-03-23.

Trial Details

NCT Number	NCT06900049
Lead Sponsor	Shanghai Jiao Tong University School of Medicine
Conditions	Duchenne Muscular Dystrophy (DMD)
Enrollment	12 participants
Start Date	2024-10-24
Primary Completion	2026-09-20 (estimated)
Study Completion	2026-12-31 (estimated)
Updated on ClinicalTrials.gov	2025-04-02