| NCT Number | NCT06725901 |
| Lead Sponsor | Universidad Nacional Andres Bello
Collaborators: Hospital Carlos Van Buren, Sociedad Chilena de Pediatría |
| Conditions | Genetic Disease, Neurogenetic Disorders |
| Enrollment | 9 participants |
| Start Date | 2024-12-10 |
| Primary Completion | 2025-10-30 (estimated) |
| Study Completion | 2025-12-30 (estimated) |
| Updated on ClinicalTrials.gov | 2025-05-29 |