| NCT Number | NCT06666816 |
| Lead Sponsor | IRCCS Eugenio Medea |
| Conditions | Muscular Dystrophies, Myopathies, Spinal Muscular Atrophy (SMA), Charcot Marie Tooth Disease |
| Enrollment | 120 participants |
| Start Date | 2017-10-27 |
| Primary Completion | 2026-12 (estimated) |
| Study Completion | 2026-12 (estimated) |
| Updated on ClinicalTrials.gov | 2026-01-20 |