Clinical Trial

An Observational Study in Children and Adults With Stargardt Disease

Active, Not Recruiting
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Summary
This multicenter, prospective, longitudinal, observational study in approximately 80 subjects with Stargardt disease secondary to biallelic mutations in the ABCA4 gene (STGD1) aims to evaluate prognostic factors of disease progression, and to further characterize the patient population for future clinical studies.
Protocol Amendment History 2 amendments
This ClinicalTrials.gov record has been amended 2 times since 2024-09-09; most recent amendment 2026-06-15.
Status change: Recruiting → Active, Not Recruiting 2026-06-15
Trial Details
NCT Number NCT06591806
Lead Sponsor AAVantgarde Bio Srl
Conditions Stargardt Disease
Enrollment 80 participants
Start Date 2024-05-01
Primary Completion 2027-06-30 (estimated)
Study Completion 2027-06-30 (estimated)
Updated on ClinicalTrials.gov 2026-06-16