Clinical Trial

Clinical Trial of Upfront Haploidentical or Unrelated Donor BMT to Restore Normal Hematopoiesis in Aplastic Anemia

Study acronym: BMT CTN CureAA
Recruiting Phase 2
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Summary
BMT CTN 2207 will investigate the use of marrow transplantation for treatment of severe aplastic anemia that has not previously been treated.
Protocol Amendment History 4 amendments
This ClinicalTrials.gov record has been amended 4 times since 2024-07-18; most recent amendment 2026-02-12.
Status change: Not Yet Recruiting → Recruiting 2025-05-06
Trial Details
NCT Number NCT06517641
Lead Sponsor Medical College of Wisconsin
Collaborators: National Heart, Lung, and Blood Institute (NHLBI), National Cancer Institute (NCI), Sanofi
Conditions Severe Aplastic Anemia
Enrollment 60 participants
Start Date 2025-05-12
Primary Completion 2028-08-01 (estimated)
Study Completion 2029-02-01 (estimated)
Updated on ClinicalTrials.gov 2026-02-17