Clinical Trial

Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I)

Active, Not Recruiting
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Summary
This Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I) is a continuation of a Phase 1/2 clinical study to evaluate the safety and efficacy of the infusion of autologous hematopoietic stem cells transduced with a lentiviral vector encoding the ITGB2 gene
Protocol Amendment History 1 amendment
This ClinicalTrials.gov record has been amended once since 2024-02-20.
Status change: Enrolling by Invitation → Active, Not Recruiting 2025-12-11
Trial Details
NCT Number NCT06282432
Lead Sponsor Rocket Pharmaceuticals Inc.
Conditions Leukocyte Adhesion Deficiency
Enrollment 9 participants
Start Date 2022-03-09
Primary Completion 2036-10-04 (estimated)
Study Completion 2036-10-04 (estimated)
Updated on ClinicalTrials.gov 2025-12-18