Clinical Trial

A Multicenter Multinational Observational Study of Children With Hypochondroplasia

Recruiting
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Summary
This study will assess growth over time and the clinical course of HCH in children by collecting growth measurements and other variables of interest.
Protocol Amendment History 5 amendments
This ClinicalTrials.gov record has been amended 5 times since 2024-01-18; most recent amendment 2025-04-01.
Trial Details
NCT Number NCT06212947
Lead Sponsor BioMarin Pharmaceutical
Conditions Hypochondroplasia
Enrollment 400 participants
Start Date 2023-11-27
Primary Completion 2043-12-31 (estimated)
Study Completion 2043-12-31 (estimated)
Updated on ClinicalTrials.gov 2025-04-03