Clinical Trial

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Recruiting
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Summary
The goal of this observational study is to characterize the epidemiology and natural history of MPS diseases by building a retrospective and prospective collection of extensive phenotypic data from French MPS patients.
Protocol Amendment History 2 amendments
This ClinicalTrials.gov record has been amended 2 times since 2023-09-12; most recent amendment 2026-02-10.
Trial Details
NCT Number NCT06036693
Lead Sponsor Institut National de la Santé Et de la Recherche Médicale, France
Conditions Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis III, Mucopolysaccharidosis IV, Mucopolysaccharidosis VI, Mucopolysaccharidosis VII, Mucopolysaccharidosis IX, Multiple Sulfatase Deficiency Disease
Enrollment 1,000 participants
Start Date 2017-12-20
Primary Completion 2026-12 (estimated)
Study Completion 2026-12 (estimated)
Updated on ClinicalTrials.gov 2026-02-11