Clinical Trial

An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics

Recruiting
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Summary
To obtain short-term and long-term clinical safety information, in pediatric and adult patients with PA and MMA treated with Carbaglu®.
Protocol Amendment History 5 amendments
This ClinicalTrials.gov record has been amended 5 times since 2021-09-09; most recent amendment 2025-04-10.
Status change: Not Yet Recruiting → Recruiting 2022-06-30
Trial Details
NCT Number NCT05040178
Lead Sponsor RECORDATI GROUP
Collaborators: Target PharmaSolutions, Inc.
Conditions Hyperammonemia, Methylmalonic Acidemia, Propionic Acidemia
Enrollment 20 participants
Start Date 2022-06-30
Primary Completion 2032-06-30 (estimated)
Study Completion 2032-06-30 (estimated)
Updated on ClinicalTrials.gov 2025-04-15