Clinical Trial

Burden of Disease and Functional Impairment in XLH

Study acronym: IdeFIX
Active, Not Recruiting
View on ClinicalTrials.gov →
Summary
Observational study comprising prospective follow up as well as retrospective chart review in order to evaluate the longitudinal course of the disease in XLH patients with a specific focus on functional impairment, physical performance and complications associated with the disease or respective treatment.
Protocol Amendment History 4 amendments
This ClinicalTrials.gov record has been amended 4 times since 2021-06-22; most recent amendment 2025-07-16.
Status change: Recruiting → Active, Not Recruiting 2023-12-05
Trial Details
NCT Number NCT04946409
Lead Sponsor Wuerzburg University Hospital
Collaborators: Kyowa Kirin, Inc.
Conditions X Linked Hypophosphatemia
Enrollment 60 participants
Start Date 2020-10-01
Primary Completion 2024-11-30 (estimated)
Study Completion 2026-10 (estimated)
Updated on ClinicalTrials.gov 2025-07-20