Clinical Trial

A Clinical Trial to Evaluate Safety of Vosoritide in At-risk Infants With Achondroplasia

Active, Not Recruiting Phase 2
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Summary
Study 111-209 is a Phase 2 randomized, open-label clinical trial of BMN 111 in infants and young children with a diagnosis of Achondroplasia at a heightened risk of requiring cervicomedullary decompression surgery
Protocol Amendment History 12 amendments
This ClinicalTrials.gov record has been amended 12 times since 2020-09-17; most recent amendment 2026-03-12.
Status change: Recruiting → Active, Not Recruiting 2022-07-26
Status change: Not Yet Recruiting → Recruiting 2020-09-25
Trial Details
NCT Number NCT04554940
Lead Sponsor BioMarin Pharmaceutical
Conditions Achondroplasia
Enrollment 20 participants
Start Date 2020-10-10
Primary Completion 2027-12 (estimated)
Study Completion 2027-12 (estimated)
Updated on ClinicalTrials.gov 2026-03-13