Clinical Trial

Long-term, Extension Study of DS-5141b in Patients With Duchenne Muscular Dystrophy

Active, Not Recruiting Phase 2
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Summary
This is a multicenter, open-label, long-term, extension, phase 2 study to evaluate the safety and efficacy of long-term treatment with DS-5141b in patients with DMD who have completed DS5141-A-J101.
Protocol Amendment History 10 amendments
This ClinicalTrials.gov record has been amended 10 times since 2020-06-12; most recent amendment 2025-09-18.
Status change: Enrolling by Invitation → Active, Not Recruiting 2021-08-18
Status change: Not Yet Recruiting → Enrolling by Invitation 2020-07-09
Trial Details
NCT Number NCT04433234
Lead Sponsor Daiichi Sankyo Co., Ltd.
Conditions Duchenne Muscular Dystrophy
Enrollment 8 participants
Start Date 2020-06-30
Primary Completion 2027-01-31 (estimated)
Study Completion 2027-01-31 (estimated)
Updated on ClinicalTrials.gov 2025-09-19