Clinical Trial

Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer

Active, Not Recruiting
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Summary
This is a long-term safety and efficacy study in subjects with CLN6 Batten disease who previously received a single intrathecal administration of AT-GTX-501.
Protocol Amendment History 5 amendments
This ClinicalTrials.gov record has been amended 5 times since 2020-02-14; most recent amendment 2025-09-29.
Status change: Recruiting → Active, Not Recruiting 2021-12-17
Trial Details
NCT Number NCT04273243
Lead Sponsor Emily de los Reyes
Conditions CLN6, Batten Disease
Enrollment 10 participants
Start Date 2020-01-24
Primary Completion 2026-12 (estimated)
Study Completion 2027-12 (estimated)
Updated on ClinicalTrials.gov 2025-10-02