| NCT Number | NCT03624374 |
| Lead Sponsor | Hugo W. Moser Research Institute at Kennedy Krieger, Inc. |
| Conditions | Leukoencephalopathies, LBSL, Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation, White Matter Disease, Ataxia, Cerebellar, Genetic Disease |
| Enrollment | 100 participants |
| Start Date | 2018-04-01 |
| Primary Completion | 2029-05 (estimated) |
| Study Completion | 2029-05 (estimated) |
| Updated on ClinicalTrials.gov | 2024-07-03 |