Clinical Trial

A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal Dystrophy

Active, Not Recruiting Phase 2/3
View on ClinicalTrials.gov →
Summary
The purpose of this study is to evaluate the efficacy and safety of RT001 in patients with Infantile Neuroaxonal Dystrophy (INAD).
Protocol Amendment History 8 amendments
This ClinicalTrials.gov record has been amended 8 times since 2018-06-25; most recent amendment 2025-06-27.
Status change: Active, Not Recruiting → Completed 2025-06-27
Status change: Enrolling by Invitation → Active, Not Recruiting 2019-07-10
Status change: Not Yet Recruiting → Enrolling by Invitation 2018-11-06
Trial Details
NCT Number NCT03570931
Lead Sponsor Biojiva LLC
Conditions Infantile Neuroaxonal Dystrophy
Enrollment 19 participants
Start Date 2018-11-05
Primary Completion 2020-08-09 (estimated)
Study Completion 2022-06-30 (estimated)
Updated on ClinicalTrials.gov 2021-10-14