Long-term safety and efficacy follow-up for participants with Hemophilia B who were previously treated in the C0371005 (formerly SPK-9001-101) study, and a dose-escalation sub-study evaluating safety, tolerability, and kinetics of a higher dose with long-term safety and efficacy follow-up. Participants in the substudy do not need to have participated in C0371005.
Protocol Amendment History
5 changes
criticalTrial completed2026-08-12
notablePrimary completion moved earlier: 2029-05-29 -> 2026-07-232026-08-12
minorCompletion moved earlier: 2029-10-25 -> 2026-07-232026-08-12