Clinical Trial

Gaucherite - A Study to Stratify Gaucher Disease

Study acronym: Gaucherite
Recruiting
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Summary
The purpose of this research is to review data already collected and to collect new data from adults and children in England with Gaucher Disease to determine clinical factors which predict severity and response to therapy of Gaucher disease especially in the areas of bone, cancer and brain conditions.
Protocol Amendment History 7 amendments
This ClinicalTrials.gov record has been amended 7 times since 2017-08-04; most recent amendment 2024-08-05.
Trial Details
NCT Number NCT03240653
Lead Sponsor Cambridge University Hospitals NHS Foundation Trust
Collaborators: Medical Research Council, National Institute for Health Research, United Kingdom
Conditions Gaucher Disease, Type I, Gaucher Disease, Type III
Enrollment 250 participants
Start Date 2014-01-01
Primary Completion 2028-09-30 (estimated)
Study Completion 2028-12-31 (estimated)
Updated on ClinicalTrials.gov 2024-08-06