Clinical Trial

Alpha/Beta T and CD19+ Depleted Peripheral Stem Cells for Patients With Primary Immunodeficiencies

Active, Not Recruiting Phase 2
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Summary
This is a Phase II trial to determine the ability of a reduced intensity conditioning regimen to allow successful engraftment with alpha/beta T and CD19+ depleted peripheral stem cell grafts from unrelated or partially matched related donors. There are two conditioning regimens depending upon patient diagnosis and age.
Protocol Amendment History 14 amendments
This ClinicalTrials.gov record has been amended 14 times since 2016-12-08; most recent amendment 2025-11-05.
Status change: Recruiting → Active, Not Recruiting 2024-12-31
Trial Details
NCT Number NCT02990819
Lead Sponsor Children's Hospital of Philadelphia
Conditions Immunodeficiencies, Immune Dysregulation Syndromes
Enrollment 60 participants
Start Date 2016-12
Primary Completion 2026-11 (estimated)
Study Completion 2027-12 (estimated)
Updated on ClinicalTrials.gov 2025-11-10