| NCT Number | NCT01193088 |
| Lead Sponsor | University of Iowa
Collaborators: National Institute of Neurological Disorders and Stroke (NINDS), Muscular Dystrophy Association, University of Rochester, University of Pennsylvania, King's College Hospital NHS Trust, Sydney Children's Hospitals Network, Children's Hospital of Philadelphia, University of Miami, Johns Hopkins University, Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta, Cedars-Sinai Medical Center, Nemours Children's Clinic, Stanford University, University of Minnesota, Massachusetts General Hospital, University of Colorado, Denver, Children's National Research Institute, University of Michigan, St. Jude Children's Research Hospital, Connecticut Children's Medical Center, Seattle Children's Hospital, The Hospital for Sick Children |
| Conditions | Charcot-Marie-Tooth Disease, Type Ia (Disorder), HMSN |
| Enrollment | 1,050 participants |
| Start Date | 2010-05 |
| Primary Completion | 2026-12 (estimated) |
| Study Completion | 2026-12 (estimated) |
| Updated on ClinicalTrials.gov | 2025-10-07 |