| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 2 | |||
| NCT07209332 | Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy | Duchenne Muscular Dystrophy | Enrolling by Invitation |
| Phase 1/2 | |||
| NCT06405633 | A Phase 1b/2a, Open-label Single Ascending Doses and Multiple Ascending Doses Study in… | Alpha-1 Antitrypsin Deficiency | Active, Not Recruiting |