Sponsor pipeline

Tippi Mackenzie clinical trial pipeline

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Data updated daily from ClinicalTrials.gov, last refresh 2026-10-16

Active trials by phase

Phase 1
1

Active trials

NCT IDTitleConditionStatusUpdated
Phase 1
NCT07479953 Prenatal Intravenous Gene Transfer With an AAV9 Vector Expressing Human… GM1 Gangliosidoses Not Yet Recruiting 2026-08-31
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