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Tippi Mackenzie clinical trial pipeline
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Data updated daily from ClinicalTrials.gov, last refresh 2026-10-16
Active trials by phase
Phase 1
1
Active trials
NCT ID
Title
Condition
Status
Updated
Phase 1
NCT07479953
Prenatal Intravenous Gene Transfer With an AAV9 Vector Expressing Human…
GM1 Gangliosidoses
Not Yet Recruiting
2026-08-31
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