Sponsor Pipeline

Tippi Mackenzie Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
1
Active Trials
0
Recruiting
Active Trials by Phase
Phase 1
1
Active Trials
NCT IDTitleConditionStatus
Phase 1
NCT07479953 Prenatal Intravenous Gene Transfer With an AAV9 Vector Expressing Human… GM1 Gangliosidoses Not Yet Recruiting
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