| First Posted | New Trial Filing | Phase | Status |
|---|---|---|---|
| 2026-07-31 | NCT07740512 Safety, Tolerability, Pharmacokinetics, and Preliminary Efficacy of PLX-200 in Pediatric… | Phase 2 | Not Yet Recruiting |
| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 3 | |||
| NCT04637282 | Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3 | Juvenile Neuronal Ceroid Lipofuscinosis | Not Yet Recruiting |
| Phase 2 | |||
| NCT07740512 | Safety, Tolerability, Pharmacokinetics, and Preliminary Efficacy of PLX-200 in Pediatric… | Lysosomal Storage Disorders | Not Yet Recruiting |