| NCT ID | Title | Condition | Status |
|---|---|---|---|
| Phase 3 | |||
| NCT04042025 | Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi | Spinal Muscular Atrophy Type I | Active, Not Recruiting |
| Not specified | |||
| NCT03421977 | Long-Term Follow-up Study for Patients From AVXS-101-CL-101 | Spinal Muscular Atrophy 1 | Active, Not Recruiting |