Sponsor Pipeline

Gemma Biotherapeutics Clinical Trial Pipeline

Data updated daily from ClinicalTrials.gov — last refresh 2026-08-16
2
Active Trials
1
Recruiting
1
Disease Areas
Active Trials by Phase
Phase 1/2
2
Active Trials
NCT IDTitleConditionStatus
Phase 1/2
NCT07070999 Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular… Spinal Muscular Atrophy Type I Recruiting
NCT04713475 Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1… GM1 Gangliosidosis Active, Not Recruiting
Disease Areas
Spinal Muscular Atrophy (1)
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